FDA Approves Novel Gene Therapy to Treat Patients with a Rare Form of Inherited Vision Loss

Luxturna is the first gene therapy approved in the U.S. to target a disease caused by mutations in a specific gene

Silver Spring, Maryland—(ENEWSPF)—December 19, 2017

By: Andrea Fischer

The U.S. Food and Drug Administration today approved Luxturna (voretigene neparvovec-rzyl), a new gene therapy, to treat children and adult patients with an inherited form of vision loss that may result in blindness. Luxturna is the first directly administered gene therapy approved in the…